Drug Solutions Podcast: Innovations in Orphan Drugs for Rare Diseases

Novel modalities and the regulatory pathways to clear their journey to patients are driving developments in rare disease treatments in 2025. In this episode of the Drug Solutions podcast, Patrick Lavery, editor for Pharmaceutical Technology®, Pharmaceutical Technology Europe^TM, and BioPharm International®, gathers perspectives from three key opinion leaders across the industry about advancements in oncology and other areas, and the increasing role of patients' families in accelerating R&D.

About the Speakers

Sarah Hein, PhD, is co-founder and CEO, March Biosciences.

Joe Katakowski, PhD, is director of research for the RTW Foundation.

Dan Williams, PhD, is co-founder, executive director, and CEO, SynaptixBio.

About the Drug Solutions Podcast

Pharmaceutical Technology presents the Drug Solutions podcast, where the editors will chat with industry experts from across the pharmaceutical and biopharmaceutical supply chain. Join us as experts share insights into your biggest questions—from the technologies, to strategies, to regulations related to the development and manufacture of drug products.

Listen to this podcast on SoundCloud, Spotify, or Apple Podcasts.